How to Help Babies Diagnosed with SMA
SMA (Spinal Muscular Atrophy) is a progressive genetic disorder that attacks motor neurons. Children with Type 1 have limited movement, trouble breathing and feeding, and with no known cure, many children with Type 1 do not live past two years old.
However, a ground-breaking treatment has recently been approved by the FDA. The treatment is one of the world’s most expensive drugs. It has a price tag upwards of $3M, leaving many families without access to this life-saving drug.